Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 Mutations: Safety and Efficacy in 15 Children and Adults Followed Up to 3 YearsJACOBSON, Samuel G; CIDECIYAN, Artur V; CONLON, Thomas J et al.Archives of ophthalmology (1960). 2012, Vol 130, Num 1, pp 9-24, issn 0003-9950, 16 p.Article

Safety in nonhuman primates of ocular AAV2-RPE65, a candidate treatment for blindness in leber congenital amaurosisJACOBSON, Samuel G; BOYE, Sanford L; CHEUNG, Andy Y et al.Human gene therapy. 2006, Vol 17, Num 8, pp 845-858, issn 1043-0342, 14 p.Article

The Human Rhodopsin Kinase Promoter in an AAV5 Vector Confers Rod- and Cone-Specific Expression in the Primate RetinaBOYE, Shannon E; ALEXANDER, John J; CLARK, Mark E et al.Human gene therapy. 2012, Vol 23, Num 10, pp 1101-1115, issn 1043-0342, 15 p.Article

Light-driven cone arrestin translocation in cones of postnatal guanylate cyclase-1 knockout mouse retina treated with AAV-GC1HAIRE, Shannon E; JIJING PANG; BOYE, Sanford L et al.Investigative ophthalmology & visual science. 2006, Vol 47, Num 9, pp 3745-3753, issn 0146-0404, 9 p.Article

Gene therapy using self-complementary Y733F capsid mutant AAV2/8 restores vision in a model of early onset Leber congenital amaurosisKU, Cristy A; CHIODO, Vince A; BOYE, Sanford L et al.Human molecular genetics (Print). 2011, Vol 20, Num 23, pp 4569-4581, issn 0964-6906, 13 p.Article

AAV-Mediated Gene Therapy for Retinal Degeneration in the rd10 Mouse Containing a Recessive PDEβ MutationPANG, Ji-Jing; BOYE, Sanford L; HAWES, Norman L et al.Investigative ophthalmology & visual science. 2008, Vol 49, Num 10, pp 4278-4283, issn 0146-0404, 6 p.Article